健康：単回投与治療が脊髄性筋萎縮症の症状を改善する
Health: Single-dose treatment improves symptoms of spinal muscular atrophy
doi: 10.1038/s41591-025-04103-w
doi: 10.1038/s41591-025-04103-w
doi: 10.1038/s41591-025-04035-5
doi: 10.1038/s41591-025-03955-6
